ISSN 2639-9431
Vol. 8, Issue 4, 2025December 05, 2025 EDT
Comparing CRISPR-Cas9 Gene Therapy Delivery Systems: Implications and Optimization for Hyperargininemia
Comparing CRISPR-Cas9 Gene Therapy Delivery Systems: Implications and Optimization for Hyperargininemia
Jad Madani, B.S., Humza N. Zubair, B.S., Ghazi A. Saroya, B.S., Rachel E.N. Reyes, Ph.D, Rami Madani, B.S.,
CRISPR/Cas9Gene TherapyArginase DeficiencyHyperargininemiaHyperammonemiaLipid nanoparticleAdeno-associated virusElectroporation
Articles in Vol. 8, Issue 4, 2025
Vol. 8, Issue 4, 2025
- Development and Characterization of Bromocriptine Mesylate Loaded Nanostructured Lipid Carriers for Enhanced Nose-to-Brain DeliveryDarshan KAAnita R DesaiMallappa ShalavadiBasavaraj S. NainegaliLaxman S Vijapur
- GIMAP and Lipid Metabolism Imaging in Clear Cell Renal Cell Carcinoma: A Negative Radiogenomic AnalysisFederico GrecoMarco CataldoAndrea PanunzioAlessandro TafuriBruno Beomonte ZobelCarlo Augusto Mallio
- A Validated Serum Biomarker Signature for the Non-Invasive Diagnosis of EndometriosisRusul F. AbediAhmed Jasim MohammedAbbas ChyadRedha Dawud Abd AlredhaGhanim A. AbbasKrarr Haider Haddawi
- Comparing CRISPR-Cas9 Gene Therapy Delivery Systems: Implications and Optimization for HyperargininemiaJad MadaniHumza N. ZubairGhazi A. SaroyaRachel E.N. ReyesRami Madani
- From BioMAG® to Feraheme®: Overview of the Intellectual Property HistoryErnest GromanDmitri Simberg
Madani, Jad, Humza N. Zubair, Ghazi A. Saroya, Rachel E.N. Reyes, and Rami Madani. 2025. “Comparing CRISPR-Cas9 Gene Therapy Delivery Systems: Implications and Optimization for Hyperargininemia.” Precision Nanomedicine 8 (4): 1634–44. https://doi.org/10.33218/001c.153885.
